Long-term efficacy and safety of eladocagene exuparvovec in patients with AADC deficiency
In: Molecular therapy, Jg. 30 (2022), Heft 2, S. 509-518
Online
serialPeriodical
Zugriff:
Titel: |
Long-term efficacy and safety of eladocagene exuparvovec in patients with AADC deficiency
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Autor/in / Beteiligte Person: | Tai, Chun-Hwei ; Lee, Ni-Chung ; Chien, Yin-Hsiu ; Byrne, Barry J. ; Muramatsu, Shin-Ichi ; Tseng, Sheng-Hong ; Hwu, Wuh-Liang |
Link: | |
Zeitschrift: | Molecular therapy, Jg. 30 (2022), Heft 2, S. 509-518 |
Veröffentlichung: | 2022 |
Medientyp: | serialPeriodical |
ISSN: | 1525-0016 (print) |
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