Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial
In: eClinicalMedicine, Jg. 65 (2023-11-01)
Online
academicJournal
Zugriff:
Titel: |
Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial
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Autor/in / Beteiligte Person: | Savarirayan, Ravi ; Hoernschemeyer, Daniel G. ; Ljungberg, Merete ; Zarate, Yuri A. ; Bacino, Carlos A. ; Bober, Michael B. ; Legare, Janet M. ; Högler, Wolfgang ; Quattrin, Teresa ; Abuzzahab, M. Jennifer ; Hofman, Paul L. ; White, Klane K. ; Ma, Nina S. ; Schnabel, Dirk ; Sousa, Sérgio B. ; Mao, Meng ; Smith, Alden ; Chakraborty, Mukta ; Giwa, Adebola ; Winding, Bent ; Volck, Birgitte ; Shu, Aimee D. ; McDonnell, Ciara |
Link: | |
Zeitschrift: | eClinicalMedicine, Jg. 65 (2023-11-01) |
Veröffentlichung: | 2023 |
Medientyp: | academicJournal |
ISSN: | 2589-5370 (electronic) |
DOI: | 10.1016/j.eclinm.2023.102258 |
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