Volltext verfügbar nach Anmeldung bzw. im Campus-Netz.
Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor
In: Scientific Reports, Jg. 11 (2021-12-01), Heft 1
Online
academicJournal
Zugriff:
Titel: |
Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor
|
---|---|
Autor/in / Beteiligte Person: | Babcock, Michael C. ; Mikulka, Christina R. ; Wang, Bing ; Chandriani, Sanjay ; Chandra, Sundeep ; Xu, Yue ; Webster, Katherine ; Feng, Ying ; Nelvagal, Hemanth R. ; Giaramita, Alex ; Yip, Bryan K. ; Lo, Melanie ; Jiang, Xuntian ; Chao, Qi ; Woloszynek, Josh C. ; Shen, Yuqiao ; Bhagwat, Shripad ; Sands, Mark S. ; Crawford, Brett E. |
Link: | |
Zeitschrift: | Scientific Reports, Jg. 11 (2021-12-01), Heft 1 |
Veröffentlichung: | 2021 |
Medientyp: | academicJournal |
ISSN: | 2045-2322 (print) |
DOI: | 10.1038/s41598-021-93601-1 |
Sonstiges: |
|